Publications

Disease impact on general well-being and therapeutic expectations of European Type II and Type III spinal muscular atrophy patients

03/06/2017
Description:

Authors: F. Rouault, V. Christie-Brown, R. Broekgaarden, N. Gusset, D. Henderson, P. Marczuk, I. Schwersenz, G. Bellis, C. Cottet .

Journal: Neuromuscular Disorders
DOI: 10.1016/j.nmd.2017.01.018

Standards of Care in spinal muscular atrophy

03/06/2017
Description:

Audience: Patient Advocacy Organizations, Europe+

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