SMA Newsroom

Clinical trialsMay 20, 2019

Novartis announced that enrollment for the ongoing clinical trial of branaplan is now closed

Novartis has sent the SMA community a letter announcing that enrollment for the ongoing clinical trial of branaplan is now closed.

Clinical trialsMay 13, 2019

Roche presented data from its risdiplam pivotal FIREFISH and SUNFISH studies at the 2019 AAN Annual Meeting

Roche presented data from two of its risdiplam trials, FIREFISH and SUNFISH, at the American Academy of Neurology annual conference.

Clinical trialsMay 9, 2019

Pre-symptomatic infants treated with Spinraza™ achieve motor milestones more consistent with normal development

Data from the NURTURE study presented at the American Academy of Neurology’s conference, showed that treatment of infantile-onset SMA (most likely to develop SMA Type 1 or 2) before the onset of symptoms resulted in motor milestone achievements more consistent with normal motor development.