News | SMA Europe - Part 30

The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. Cure SMA Annual Conference

    Cure SMA held its annual conference in June in Kansas City, where six representatives of the drug programs currently being assessed in clinical trials presented their work. The SMN protein has two identical variants – SMN1 and SMN2. SMN2 is mainly produced as an unstable and shortened version of the SMN protein due to a […]