SMA Newsroom

Clinical trialsMay 9, 2019

AveXis presents positive interim results on Zolgensma across a broad spectrum of patients with SMA

AveXis presented positive results from clinical trials on Zolgensma, across a broad spectrum of patients with SMA at the 2019 American Academy of Neurology conference in Philadelphia.

ResearchMay 9, 2019

Potential biomarker for SMA identified

Biogen presented data at the American Academy of Neurology 2019 conference on a potential biomarker for SMA. Biomarkers provide insight on disease progression.

Clinical trialsFeb 27, 2019

Scholar Rock Announced Positive Interim Results from Phase 1 Trial of SRK-015 in Healthy Volunteers and Updates on Future Development Plans

Scholar Rock announced positive interim results from the ongoing Phase 1 clinical trial of its potential muscle-targeted SMA therapy, SRK-015 in healthy adult volunteers.