Isis Pharmaceuticals announced the official launch of an open-label extension study, called SHINE, which will be continuing treatment of the same infants and children diagnosed with SMA who had previously participated in Phase III studies ENDEAR and CHERISH. The infants who participated in ENDEAR will continue to receive 12mg of ISIS-SMNRx every 4 months, while […]
The University of Aberdeen has announced that researchers have made a significant breakthrough in understanding SMA. Funding for this research came in part from one of our member organisations, The SMA Trust. Vanessa Christie-Brown, Research Co-ordinator at The SMA Trust commented “We are delighted to have funded Professor Parson’s work on vascular involvement in SMA. […]
The CURE-SMA annual conference is the largest SMA conference in the world. Through the conference, researchers, healthcare professionals and families are all brought together to network, learn and collaborate. The family conference includes a variety of workshops, keynote sessions with leading researchers, a family-friendly research poster session and more—plus fun events like the dance party, […]
The conference will once again be hosted jointly by the MRC Centre for Neuromuscular Diseases and Muscular Dystrophy UK. Registration is now open. The fee is £250 and includes a Gala Dinner. Venue: Medical Sciences Teaching Centre, Oxford. For more information, please click here.
The fifth International Congress of Myology will be held between 14th and 18th March in the Lyon Conference Centre, Lyon, France. The best specialists in this emerging discipline from the five continents are expected to present and challenge their latest findings, not only in fundamental research but also in clinical science and therapeutics. For more […]