News

The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. A Biogen community update on Spinraza NURTURE study

    Based on our request for an update, Biogen has provided us with the following information about new results from their NURTURE study, a study of pre-symptomatic patients with SMA, recently presented at the virtual Cure SMA Research & Clinical Care Meeting, which took place from 10th to 12th June 2020. NURTURE is an ongoing, Phase […]

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  2. Scholar Rock reports delays in interim trial results due to COVID-19

    Scholar Rock reported on the recent progress and upcoming milestones for the TOPAZ Phase 2 clinical trial of SRK-015 in patients with Type 2 or 3 SMA, in the light of the COVID-19 pandemic. SRK-015 is a muscle-directed therapy that aims to reverse or restrict the muscle atrophy and weakness experienced by SMA patients. The drug is […]

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  3. DEVOTE Trial – First patient treated

    Based on our request for an update, Biogen has provided us with the following information on its global clinical study DEVOTE. The study is designed to evaluate the safety, tolerability and potentially improved efficacy of nusinersen when administered at a higher dose than currently approved for the treatment of SMA. The Phase 2/3 randomised, controlled, […]

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