The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. Financial boost to develop promising regenerative treatments for neuromuscular diseases

    The Spinal Muscular Atrophy (SMA) Foundation and PTC Therapeutics have entered into a new collaboration focused on regenerative medicine to further advance scientific research in SMA and other neuromuscular disorders. Recent FDA approvals of several disease modifying therapies for SMA have made regenerative medicine approaches the next frontier in drug discovery and development. These approved […]


  2. UK SMA Research Online Conference – 10th & 11 September 2020

    Save the date for the UK SMA Research Online Conference, which will take place on 10th & 11th September between 1 and 4.30pm GMT. A committee of UK-based PhD students have got together to organise this event with the aim of giving early career researchers (ECRs) an opportunity to present their work. There will be […]