The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.
The Spinal Muscular Atrophy (SMA) Foundation and PTC Therapeutics have entered into a new collaboration focused on regenerative medicine to further advance scientific research in SMA and other neuromuscular disorders. Recent FDA approvals of several disease modifying therapies for SMA have made regenerative medicine approaches the next frontier in drug discovery and development. These approved […]
Professor Brunhilde Wirth, Chair of the Institute of Human Genetics at the University Hospital of Cologne, Germany and Chair of our Scientific Advisory Board (SAB), has published a comprehensive review on the genetics of SMA and how the path from gene discovery to therapy in SMA has been a highly challenging endeavour, but also led […]
SMA Europe is delighted to announce that it has partnered with an international SMA research training network, led by Prof. Dr. rer. nat. Peter Claus in Hannover in Germany. This initiative, SMA BEYOND, has been granted a €2.14M Horizon 2020 award by the European Commission. Over four years, early-stage researchers, based in 8 laboratories in […]
Six dedicated young PhD students from institutions across the UK are organising an online SMA research conference on 10th & 11th September. Find out more about them, their work and their interests outside the laboratory! INES BOEHM Ines completed her BSc in Molecular Biology from the University of Salzburg and Johannes Keppler University Linz (Austria), […]
Save the date for the UK SMA Research Online Conference, which will take place on 10th & 11th September between 1 and 4.30pm GMT. A committee of UK-based PhD students have got together to organise this event with the aim of giving early career researchers (ECRs) an opportunity to present their work. There will be […]