The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. EMA to hold stakeholder workshop for SMA

    Following a request by SMA Europe, the European Medicines Agency (EMA) will host a one-day workshop on spinal muscular atrophy (SMA) on 11th November this year, at its headquarters in London to allow SMA stakeholders to have an open forum discussion on the current challenges that face therapy development for SMA. This initiative is very important as […]


  2. Study shows impaired endocytosis in SMA & a potential new treatment strategy.

    The Chair of our Scientific Advisory Board, Professor Brunhilde Wirth of the University of Cologne, published an important paper in the American Journal of Human Genetics. This study, partly funded by SMA Europe, unravels impaired endocytosis in SMA. Endocytosis is a mechanism used by cells to recycle and transport molecules by engulfing them. This is […]


  3. Call for SMA research proposals 2016 now open!

    We are delighted to announce that we have launched our 9th Call for SMA Research Proposals. To find out more about the Call, our eligibility criteria and how to apply, please read our launch document. To access the application portal (hosted by AFM Téléthon), please click here and follow “SMA Europe 9th Call for Proposals”. We […]