Our Clinical Trial Readiness Project

As part of its mission to bring effective therapies to patients in a timely & sustainable way, SMA Europe has joined Cure SMA and the Industry Consortium, to understand and expand Europe’s current capacity to run clinical trials for potential SMA therapies.

In order to achieve this, several initiatives have been undertaken, starting with a survey to better understand the current landscape in Europe.

An analysis of the data obtained indicated that sites would value educational material and training opportunities to increase their capacity to run clinical trials for SMA in their countries. We have therefore engaged in the following activities: