Project archive

The purpose of SMA Europe is to provide a framework to stimulate collaboration

and accelerate translational research pathways in SMA and promote patient care.

Optimization of AAV9-SMN gene therapy for SMA

Principal investigator(s):
Dr. Martine Barkats
Institution:
Institut de Myologie, INSERM, France
Grant:
192,764€
Grant Type:
Operating Grant
Call number:
5
Start year:
2013
Duration:
2 years
Status:
Ended

Using RNA secondary structure as a therapeutic target for Spinal Muscular Atrophy: a new drug discovery approach

Principal investigator(s):
Dr. Amparo Garcia-Lopez
Institution:
University of Geneva, Switzerland
Grant:
Grant Type:
Fellowship
Call number:
6
Start year:
2014
Duration:
2 years
Status:
Half way through

Modulating SMN2 splicing with dual inhibitors of Sam68 and hnRNP A1: A novel therapeutic approach for Spinal Muscular Atrophy

Principal investigator(s):
Professor Eduardo Tizzano
Institution:
Hospital de la Santa Creu i Sant Pau, Barcelona, Spain
Grant:
Grant Type:
Operating grant
Call number:
6
Start year:
2014
Duration:
2 years
Status:
Half way through