New publication: Systematic Literature Review of the Natural History of Spinal Muscular Atrophy. Motor Function, Scoliosis, and Contractures.
Background and Objectives of the publication.
Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder associated with continuous motor function loss and complications, such as scoliosis and contractures. Understanding the natural history of SMA is key to demonstrating the long-term outcomes of SMA treatments. This study reviews the natural history of motor function, scoliosis, and contractures in patients with SMA.