Community update from Roche
We are pleased to share with you the latest community update issued by Roche.
It contains the information shared at the Cure SMA Research & Clinical Care Meeting 2023 and Family Conference which took place last week.
Presentations at Cure SMA Research & Clinical Care Meeting June 28 – 30, 2023 included topics such as:
- Long-term efficacy and safety of risdiplam
- Real-world evidence generation:
- Results from a study assessing real-world outcomes among patients with SMA who have been treated with risdiplam were presented.
- The design for a post-authorisation effectiveness study (PAES) in patients with SMA treated with risdiplam in real-world settings.