Promoting and generating patient-relevant evidence to support evidence-based patient advocacy.
Ensuring the needs and wants of patients across Europe are taken into account during the entire drug development process
Generating evidence on the access situation to diagnosis, treatment and care in Europe
All together. One goal.
Our members are national patient organisations led by people living with SMA and their families. Together, we are determined to make a positive difference to the lives of all those who are also living with SMA.
SMA Europe initiatives
Working to bring effective treatments and optimal care to everyone living with SMA
Revealing the 'quest to access' of people living with SMA
Making Newborn Screening for SMA a reality in all European countries