Projects

The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. AAV9-mediated gene therapy in murine and feline models of SMA

    Principal investigator(s) :
    Dr. Martine Barkats
    Institution :
    INSERM, Paris, France
    Grant :
    164,725€
    Grant Type:
    Operating Grant
    Call number :
    3
    Start year :
    2011
    Status :
    Not yet started