The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. Modulating SMN2 splicing with dual inhibitors of Sam68 and hnRNP A1: A novel therapeutic approach for Spinal Muscular Atrophy

    Principal investigator(s) :
    Professor Eduardo Tizzano
    Institution :
    Hospital de la Santa Creu i Sant Pau, Barcelona, Spain
    Grant :
    Grant Type:
    Operating grant
    Call number :
    Start year :
    Duration :
    2 years
    Status :
    Half way through