Modulating SMN2 splicing with dual inhibitors of Sam68 and hnRNP A1: A novel therapeutic approach for Spinal Muscular Atrophy
Principal investigator(s) :
Professor Eduardo Tizzano
Institution :
Hospital de la Santa Creu i Sant Pau, Barcelona, Spain
Grant :
€
Grant Type:
Operating grant
Call number :
6
Start year :
2014
Duration :
2 years
Status :
Half way through
