Projects

The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. Optimization of AAV9-SMN gene therapy for SMA

    Principal investigator(s) :
    Dr. Martine Barkats
    Institution :
    Institut de Myologie, INSERM, France
    Grant :
    192,764€
    Grant Type:
    Operating Grant
    Call number :
    5
    Start year :
    2013
    Duration :
    2 years
    Status :
    Ended