“SMA Europe online tool helps patients find clinical trials” published by SMA News Today
We are delighted to invite you to read the latest article on our Clinical Trials Finder website by SMA News Today.
SMA Newsroom
Sep 30, 2025
“SMA Europe Launched New Clinical Trials Finder to Support Access to Clinical Trials and Accelerate Progress in SMA Treatment” published by Rare Revolution Magazine.
We are delighted to invite you to read the latest article on our Clinical Trials Finder website by Rare Revolution Magazine.
Sep 24, 2025
Community Update: FDA decision on the high-dose regimen of nusinersen in the treatment of SMA.
Today, Biogen announced that the U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) for its supplemental New Drug Application for a high-dose regimen of nusinersen in the treatment of SMA.
Sep 23, 2025
Community Update: FDA decision on the approval of Scholar Rock's apitegromab
Today, Scholar Rock announced that the U.S. Food and Drug Administration (FDA) has delayed approval of the Biologics License Application (BLA) for apitegromab in the treatment of people living with SMA.