The following text aims to clarify the current situation regarding Zolgensma global Managed Access Program after the changes announced by NGTx on the 9th of January 2023.

2022 brought us many challenges and opportunities and we could not be more grateful for all the support we have received to approach those.

It would not be possible without the SMA Community who accompany us at each step of this adventure. We believe that, together, we can have a real impact and achieve sustainable change.

We are pleased to share with you the latest community statement issued by Roche that gives an interesting overview of last year's achievements.

Please read the latest CRA report on newborn screening in Europe.