SMA Newsroom

TreatmentsMar 21, 2025

Community update from Roche: Final five-year data from the pivotal SUNFISH (NCT02908685) study

Roche shared updates on the final results of the now-concluded SUNFISH study, which assessed the efficacy and safety of risdiplam in people living with SMA aged 2-25 years.

TreatmentsMar 21, 2025

Community update from Novartis: Phase III STEER and Phase IIIb STRENGTH studies

Novartis shared updates on the results from Phase III STEER and Phase IIIb STRENGTH studies, evaluating intrathecal onasemnogene abeparvovec (OAV101 IT) in people living with SMA aged two to <18 years. 

TreatmentsDec 20, 2024

Community Update Biohaven: RESILIENT Letter to SMA Community

Biohaven released the results from their RESILIENT SMA clinical trial, and they did not meet the primary endpoint. Biohaven is currently analysing the data further and is engaging in discussion with Health Authorities.