SMA Newsroom

ResearchNov 9, 2022

SMA Priority Setting Project

We launch SMA Priority Setting Project!

Clinical trialsOct 27, 2022

Scholar Rock: New Phase 2 TOPAZ Trial Data

Scholar Rock has recently issued a press release regarding New Phase 2 TOPAZ Trial Data.

OtherOct 18, 2022

Novartis Community Update September 2022

In this September 2022 community update, Novartis Gene Therapies shares the latest updates on SMA Clinical Trial Program. 

For more information please see the link below.

ResearchOct 13, 2022

New two-year data from the JEWELFISH study evaluating Evrysdi (risdiplam)

Roche announces new two-year data from the JEWELFISH study evaluating Evrysdi (risdiplam) in people with Type 1, 2 or 3 SMA aged 6 months to 60 years at the time of enrolment. The data will be first presented at the 27th World Muscle Society (WMS) congress, 11-15 October 2022. 

It will be also announced during the Roche PAG Scientific Meeting taking place during our 3rd Scientific Congress on Spinal Muscular Atrophy in Barcelona on Saturday, 22 October at 4 pm.