SMA Newsroom

End of Year 2023 Roche's Community Letter

End of Year 2023: Roche's Community Letter

We are pleased to share with you the latest Community Update from Roche.&nbsp;

End of Year 2023: Roche's Community Update

Full article

"I am Unique": Rarity Life Magazine article on the 2023 Awareness Campaign

We are delighted to share with all of you the latest article about our 2023 Awareness Campaign: "I am Unique".

New article: "I am Unique"

Full publication

Systematic Literature Review of the Natural History of Spinal Muscular Atrophy

Background and Objectives of the publication.
Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder associated with continuous motor function loss and complications, such as scoliosis and contractures. Understanding the natural history of SMA is key to demonstrating the long-term outcomes of SMA treatments. This study reviews the natural history of motor function, scoliosis, and contractures in patients with SMA.

New publication: Systematic Literature Review of the Natural History of Spinal Muscular Atrophy. Motor Function, Scoliosis, and Contractures.

Full Press Release

risdiplam

Evrysdi™

We are pleased to announce that, in response to our standing request for important SMA clinical development and programme updates, Roche has shared an update on the RAINBOWFISH clinical trial, for which results from the primary analysis were presented at the 28th World Muscle Society (WMS) Congress.

Categories