SMA Newsroom

Link to the open access article

<p>Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study.</p>
<p>Outcome measures traditionally used in spinal muscular atrophy (SMA) clinical trials are inadequate to assess the full range of disease severity. The aim of this study was to assess the psychometric properties of a set of existing questionnaires and new items, gathering information on the impact of SMA from the patient and caregiver perspectives.</p>

New publication: Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy.

Whitepaper in Spanish and Portuguese

<p>You can now find new translations of Newborn Screening Alliance Whitepaper in Spanish and Portuguese.</p>

Newborn Screening Alliance: Whitepaper in Spanish and Portuguese

Register here

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<div data-offset-key="ui0u-0-0">Roche, in collaboration with SMA Europe, is hosting the &lsquo;Nutrition in SMA&rsquo; workshop with an expert panel of HCPs and patient representatives, to discuss the challenges surrounding nutritional care in SMA.</div>
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<div data-offset-key="ui0u-0-0">Join the discussion!</div>
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SMA Newsroom

New publication: Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy.

Newborn Screening Alliance: Whitepaper in Spanish and Portuguese

"Nutrition in SMA" workshop, 21st November

SMA Priority Setting Project

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