SMA Newsroom

TreatmentsJul 20, 2023

Community statement: BIOCAD

Biocad, a Russian biotechnology company, shares a community statement on its gene therapy product, ANB-004, which is being developed to treat SMA.

OtherJul 7, 2023

Community update from Roche

We are pleased to share with you the latest community update issued by Roche.

It contains the information shared at the Cure SMA Research & Clinical Care Meeting 2023 and Family Conference which took place last week.

Clinical trialsJun 30, 2023

Scholar Rock announces new data from the Phase 2 TOPAZ trial extension period evaluating patient outcomes at 36 months of treatment with apitegromab.

Scholar Rock announces new data from the Phase 2 TOPAZ trial extension period evaluating patient outcomes at 36 months of treatment with apitegromab.