SMA Newsroom

OdySMASep 20, 2022

Laura Gumbert, our OdySMA Project Manager, selected as a recipient of the ISPOR Patient Representative Conference Grant.

Laura Gumbert, our OdySMA Project Manager, has been selected as a recipient of the ISPOR Patient Representative Conference Grant for Virtual ISPOR Europe 2022.

Clinical trialsSep 20, 2022

Community update Scholar Rock: SAPPHIRE clinical trial sites in Europe

A community update has been shared by Scholar Rock regarding the sites for SAPPHIRE clinical trials in Europe. 

The SAPPHIRE study intends to enroll approximately 204 individuals with SMA across Europe and the USA. The plan is to have European trial sites in Belgium, France, Germany, Italy, Netherlands, Poland, Spain, and the United Kingdom. 

Scholar Rock has begun enrolling patients in Europe, with the first clinical trial sites up and running in Spain. The team is working on opening additional sites.

OtherSep 19, 2022

News on positive developments for SMA newborn screening in Spain and Denmark

Last week, new positive news was announced by governments in Spain and Denmark.

Please see below to read more.