Community Update Roche: EMA approval of the risdiplam tablet
We are pleased to share a community letter from Roche, announcing that the European Commission (EC) has approved a new, room- temperature stable tablet formulation of risdiplam.
SMA Newsroom
New publication: Spinal cord stimulation: A new perspective for SMA research by Rare Revolution Magazine.
We are delighted to invite you to read the latest Spinal cord stimulation: A new perspective for SMA research by Rare Revolution Magazine.
SMA News Today latest article: "SMA Europe’s inaugural gathering to discuss medical emergencies"
We're excited to announce that SMA News Today has featured our 1st International Clinical Care Symposium on SMA, as part of their latest publication!
TreatmentsMar 28, 2025
Community update from Scholar Rock
Scholar Rock announced that the FDA has granted priority review for the Biologics License Application for apitegromab, an investigational muscle-targeted treatment developed to improve motor function for people living with SMA who are receiving an SMN-targeted treatment.