The purpose of SMA Europe is to provide a framework to stimulate collaboration and accelerate translational research pathways in SMA and promote patient care.

  1. The patient voice at EMA

    The European Medicines Agency (EMA) is the European Union agency responsible for the evaluation and supervision of medicines.

    Hear the voices of EMA’s stakeholders – Patients and healthcare professionals representatives explain the value of working with the Agency for better decision-making and how important it is to ensure your voice is added to the regulatory dialogue.

    SMA Europe, as a stakeholder at EMA, held a workshop in November 2016 to allow SMA stakeholders, patients, doctors, industry representatives, researchers and regulators, to have an open forum discussion on the current challenges that face therapy development for SMA.